Found 4 matching trials
Clinical Trial to Assess the Safety and Efficacy of EXG001-307 in Patients With Spinal Muscular Atrophy
EARLY_PHASE1The purpose of this trial is to evaluate safety and efficacy of intrathecal...
Status
Enrolling By Invitation
Location
Shanghai Children's Medical Center Affiliated to Shanghai Jiao Tong University School of Medicine
A Long-term Follow-up Study Evaluating Intravenous Injection of EXG001-307 in Patients With Type 1 SMA
N/AAn Open-label, Long-term Follow-Up Study to Evaluate the Safety and Tolerab...
Status
Enrolling By Invitation
Location
The Children's Hospital of Fudan University
Clinical Trial to Assess the Safety and Efficacy of EXG001-307 in Patients with Spinal Muscular Atrophy Type 1
PHASE1The purpose of this trial is to evaluate safety and efficacy of intravenous...
Status
Enrolling By Invitation
Location
The Children's Hospital of Fudan University
Clinical Trial to Evaluate the Safety and Efficacy of EXG001-307 in Patients With Spinal Muscular Atrophy Type I
EARLY_PHASE1The purpose of this study was to evaluate the safety and preliminary effica...
Location
Hangzhou Jiayin Biotechnology Co., Ltd